An Extension Study of Subjects Who Received an Avalyn Inhaled Antifibrotic Agent (SAIL)

Part of paid clinical trials in Birmingham, Alabama.

Sponsor
Avalyn Pharma Inc.
Study ID
NCT06951217
Phase
PHASE2
Status
Recruiting

Conditions

  • Idiopathic Pulmonary Fibrosis (IPF)
  • Progressive Pulmonary Fibrosis

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

  • AP01 — COMBINATION_PRODUCT
    AP01 will be administered open-label via the eFlow Nebulizer System

Study Details

This is an open-label extension study for participants who were previously enrolled in and completed an Avalyn Pharma Sponsored study with an inhaled antifibrotic, such as AP01. Eligible participants will have their final dose of drug at the end of study visit from the lead-in study and first AP-LTE-008 study visit on the same day.

Key Dates

Start date
Apr 17, 2025
Status verified
Feb 2026
Primary completion
Dec 31, 2031
Completion
Dec 31, 2031

Study Design

Enrollment
340 participants (estimated)
Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT

Arms

  • Experimental: Open-label AP01 treatment arm
    All trial participants will enroll from a Sponsor-led parent study of AP01 and receive open-label AP01 for continued evaluation of long-term safety and tolerability.

Primary Outcome Measure

To evaluate the long-term safety and tolerability outcomes of subjects receiving Avalyn nebulized antifibrotic medications (AP01). [ Time Frame: Through end of study; average of 6 years ]

Central Contacts

Locations (23)

FacilityCityStateZIPSite coordinators
University of Alabama at BirminghamBirminghamAlabama35205
Tejaswini Kulkarni (PRINCIPAL_INVESTIGATOR)
University of Southern CaliforniaLos AngelesCalifornia90033
Toby Maher (PRINCIPAL_INVESTIGATOR)
University of Colorado, Anschutz Medical CampusAuroraColorado80045
Joyce Lee
Joyce Lee, MD (PRINCIPAL_INVESTIGATOR)
Renstar Medical ResearchOcalaFlorida34470
Raj Karunakara
Raj Karunakara, MD (PRINCIPAL_INVESTIGATOR)
Piedmont Healthcare, Inc.AtlantaGeorgia30309
Amy Case
Amy Case, MD (PRINCIPAL_INVESTIGATOR)
University of MarylandBaltimoreMaryland21201
Edward Britt (PRINCIPAL_INVESTIGATOR)
Mayo Clinic RochesterRochesterMinnesota55901
Andrew Limper
Sam Nascak
Andrew Limper, MD (PRINCIPAL_INVESTIGATOR)
Hannibal Regional Healthcare System, Inc.HannibalMissouri63401
Humam Farah, MD
Humam Farah, MD (PRINCIPAL_INVESTIGATOR)
Columbia UniversityNew YorkNew York10032
Claire McGroder
Claire McGroder, MD (PRINCIPAL_INVESTIGATOR)
Icahn School of Medicine at Mount SinaiNew YorkNew York10029
Maria Padilla
Maria Padilla, MD (PRINCIPAL_INVESTIGATOR)
Piedmont HealthCare, PAStatesvilleNorth Carolina28625
Jose Perez
Jose Perez, MD (PRINCIPAL_INVESTIGATOR)
Southeastern Research CenterWinston-SalemNorth Carolina27103
Jason Thomason
336-765-0383
Jason Thomason, MD (PRINCIPAL_INVESTIGATOR)
University of CincinnatiCincinnatiOhio45267
Nishant Gupta
Nishant Gupta, MD (PRINCIPAL_INVESTIGATOR)
The University of Kansas Medical CenterKansasOhio66160
Mark Hamblin
Mark Hamblin, MD (PRINCIPAL_INVESTIGATOR)
Summit HealthBendOregon97701
Jeremy Feldman, MD
Jeremy Feldman, MD (PRINCIPAL_INVESTIGATOR)
Temple University HospitalPhiladelphiaPennsylvania19140
Gerard Criner, MD
Gerard Criner, MD (PRINCIPAL_INVESTIGATOR)
Thomas Jefferson UniversityPhiladelphiaPennsylvania19107
Ross Summer
Ross Summer, MD (PRINCIPAL_INVESTIGATOR)
Lowcountry Lung and Critical Care, PACharlestonSouth Carolina29406
Thomas Kaelin, Jr, DO
Thomas Kaelin, Jr., DO (PRINCIPAL_INVESTIGATOR)
Medical University of South CarolinaCharlestonSouth Carolina29425
Timothy Whelan
Timothy Whelan, MD (PRINCIPAL_INVESTIGATOR)
Vanderbilt University Medical CenterNashvilleTennessee37204
Justin Hewlett, MD
Justin Hewlett, MD (PRINCIPAL_INVESTIGATOR)
El Paso Pulmonary Association, P.A.El PasoTexas79902
Carlo Hatem, MD
Carlo Hatem, MD (PRINCIPAL_INVESTIGATOR)
Intermountain Medical CenterMurrayUtah84107
Peter Crossno, MD
Peter Crossno, MD (PRINCIPAL_INVESTIGATOR)
Inova HealthcareFalls ChurchVirginia22042
Vikramjit Khangoora (PRINCIPAL_INVESTIGATOR)

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