Duchenne Muscular Dystrophy — Trials, FDA Actions & Pivotal Research

20 active Duchenne Muscular Dystrophy trials currently recruiting in the US, sourced from ClinicalTrials.gov.

Synced daily from openFDA and ClinicalTrials.gov. Last sync: June 12, 2026.

Recruiting trials by city

Cities where Duchenne Muscular Dystrophy trials in our archive had recruiting sites. Each link lists every currently recruiting paid clinical trial at that location.

Little Rock, AR Boston, MA Gainesville, FL Aurora, CO Chicago, IL Los Angeles, CA Sacramento, CA

Active Duchenne Muscular Dystrophy trials

Currently recruiting US trials matching Duchenne Muscular Dystrophy, sourced live from ClinicalTrials.gov. We’ll add per-event articles here as those trials post results or hit primary completion.

Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting

for Duchenne Muscular Dystrophy

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: 4+

Code: NCT07542314·Phase 4·Not Yet Recruiting

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

for Muscular Dystrophies

Sponsor: Avidity Biosciences, Inc.

Sex: Male·Age: 7 - 16

Code: NCT07587242·Phase 3·Not Yet Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

for Duchenne Muscular Dystrophy (DMD)

1 location in Hillsborough

Sponsor: Dyne Therapeutics

Sex: Male·Age: 4 - 18

Code: NCT07608432·Phase 3·Recruiting

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Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Wave Life Sciences USA, Inc.

Sex: Male·Age: All ages

Code: NCT07209332·Phase 2·Enrolling By Invitation

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

for Duchenne Muscular Dystrophy

7 locations incl. Los Angeles

Sponsor: Satellos Bioscience, Inc.

Sex: Male·Age: 7 - 9

Code: NCT07287189·Phase 2·Recruiting

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A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

for Duchenne Muscular Dystrophy

3 locations incl. Little Rock

Sponsor: Solid Biosciences Inc.

Sex: Male·Age: 7 - 11

Code: NCT07160634·Phase 3·Recruiting

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A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.

for DMD

Sponsor: Belief BioMed (Beijing) Co., Ltd

Sex: Male·Age: 4 - 9

Code: NCT07058662·Phase 1, Phase 2·Recruiting

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A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

for Duchenne Muscular Dystrophy

10 locations incl. Little Rock

Sponsor: Insmed Gene Therapy LLC

Sex: Male·Age: 2 - 4

Code: NCT06817382·Phase 1·Recruiting

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Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Başak Çağla Arslan

Sex: Male·Age: 13 - 18

Code: NCT06402942·Recruiting

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Trial of Cell Based Therapy for DMD

for Duchenne Muscular Dystrophy

1 location in Minneapolis

Sponsor: Masonic Cancer Center, University of Minnesota

Sex: All·Age: 18+

Code: NCT06692426·Phase 1·Recruiting

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Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy

for Executive Dysfunction

Sponsor: Lokman Hekim University

Sex: Male·Age: 6 - 12·Accepts healthy volunteers

Code: NCT06868784·Enrolling By Invitation

Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.

for Duchenne Muscular Dystrophy

Sponsor: University of Malaga

Sex: All·Age: 5 - 20

Code: NCT06363526·Enrolling By Invitation

Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old

for Duchenne Muscular Dystrophy

Sponsor: Italfarmaco

Sex: Male·Age: 2 - 6

Code: NCT06769633·Phase 2·Recruiting

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Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Assiut University

Sex: Male·Age: 5 - 18·Accepts healthy volunteers

Code: NCT06732011·Not Yet Recruiting

The U.K. NorthStar Clinical Network

for Duchenne Muscular Dystrophy

Sponsor: University College, London

Sex: Male·Age: Up to 99

Code: NCT06711692·Not Yet Recruiting

Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Sex: Male·Age: All ages

Code: NCT06579859·Not Yet Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

for Duchenne Muscular Dystrophy

25 locations incl. Phoenix

Sponsor: Catalyst Pharmaceuticals, Inc.

Sex: Male·Age: 2+

Code: NCT06564974·Recruiting

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Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies

for Duchenne Muscular Dystrophy

Sponsor: University of Haifa

Sex: Male·Age: 14 - 30

Code: NCT06540365·Not Yet Recruiting

ML-Based Multi-Sensor Fall Risk Screening in DMD

for DMD

Sponsor: Seoul National University Hospital

Sex: All·Age: 10 - 30

Code: NCT07015632·Recruiting

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Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

for Duchenne Muscular Dystrophy

1 location in Nashville

Sponsor: Vanderbilt University Medical Center

Sex: Male·Age: 10+

Code: NCT06093100·Recruiting

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