Adrenoleukodystrophy — Trials, FDA Actions & Pivotal Research

10 active Adrenoleukodystrophy trials currently recruiting in the US, sourced from ClinicalTrials.gov.

Synced daily from openFDA and ClinicalTrials.gov. Last sync: June 12, 2026.

Recruiting trials by city

Cities where Adrenoleukodystrophy trials in our archive had recruiting sites. Each link lists every currently recruiting paid clinical trial at that location.

Los Angeles, CA

Active Adrenoleukodystrophy trials

Currently recruiting US trials matching Adrenoleukodystrophy, sourced live from ClinicalTrials.gov. We’ll add per-event articles here as those trials post results or hit primary completion.

IT and IV Lentiviral Gene Therapy for X-ALD

for X-linked Adrenoleukodystrophy

Sponsor: Shenzhen Geno-Immune Medical Institute

Sex: All·Age: 1 - 60

Code: NCT03727555·Recruiting

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Disease Progression in Women With X-linked Adrenoleukodystrophy

for X-linked Adrenoleukodystrophy

Sponsor: Minoryx Therapeutics, S.L.

Sex: Female·Age: 18+

Code: NCT06178120·Recruiting

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Validation of a Prognostic Biomarker Using Brain Diffusion MRI in X-linked Adrenoleukodystrophy

for X-linked Adrenoleukodystrophy

Sponsor: Assistance Publique - Hôpitaux de Paris

Sex: All·Age: 18+·Accepts healthy volunteers

Code: NCT05911919·Not Yet Recruiting

Registry of X-linked Adrenoleukodystrophy

for X-linked Adrenoleukodystrophy

Sponsor: Beijing Tiantan Hospital

Sex: All·Age: 6 - 70·Accepts healthy volunteers

Code: NCT05939232·Recruiting

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Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia

for Adrenoleukodystrophy

Sponsor: Assistance Publique - Hôpitaux de Paris

Sex: All·Age: 15 Months - 60·Accepts healthy volunteers

Code: NCT04925349·Recruiting

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Quality of Life in Women with X-linked Adrenoleukodystrophy

for X-linked Adrenoleukodystrophy

Sponsor: Leipzig University Medical Center

Sex: Female·Age: 18+

Code: NCT04675749·Recruiting

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Adrenoleukodystrophy National Registry Study

for ALD (Adrenoleukodystrophy)

1 location in Minneapolis

Sponsor: Masonic Cancer Center, University of Minnesota

Sex: All·Age: All ages

Code: NCT03789721·Recruiting

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The Myelin Disorders Biorepository Project

for Leukodystrophy

23 locations incl. Los Angeles

Sponsor: Children's Hospital of Philadelphia

Sex: All·Age: All ages

Code: NCT03047369·Recruiting

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UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

for Adrenoleukodystrophy

1 location in Durham

Sponsor: Joanne Kurtzberg, MD

Sex: All·Age: 1 Week - 22

Code: NCT02254863·Phase 1·Recruiting

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Longitudinal Study of Neurodegenerative Disorders

for MLD

1 location in Pittsburgh

Sponsor: University of Pittsburgh

Sex: All·Age: All ages

Code: NCT03333200·Recruiting

Apply to this trial