Disease Progression in Women With X-linked Adrenoleukodystrophy
- Sponsor
- Minoryx Therapeutics, S.L.
- Study ID
- NCT06178120
- Status
- Recruiting
Conditions
Eligibility Criteria
- Sex
- FEMALE
- Age
- 18 Years - N/A
- Healthy Volunteers
- Not accepted
Study Details
Observational, single-site prospective and minimally interventional study in women with X-linked adrenoleukodystrophy (ALD), conducted in France.
Key Dates
- Start date
- Jan 2, 2024
- Status verified
- Dec 2023
- Primary completion
- Dec 31, 2026
- Completion
- Jun 30, 2027
Study Design
- Enrollment
- 40 participants (estimated)
Primary Outcome Measure
Spinal cord magnetization transfer ratio (MTR) [ Time Frame: Change from baseline up to 2 years ]
Central Contacts
- Arun Mistry+34935441466
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