A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
for Spinal Muscular Atrophy (SMA)
17 locations incl. Little Rock
Sponsor: argenx
Sex: All·Age: 5 - 17
Code: NCT07287982·Phase 2·Recruiting