Trial of Nadofaragene Firadenovec vs. Observation in Participants With Intermediate Risk Non-Muscle Invasive Bladder Cancer

Part of paid clinical trials in Mobile, Alabama.

Sponsor
Ferring Pharmaceuticals
Study ID
NCT06510374
Phase
PHASE3
Status
Recruiting

Conditions

  • Intermediate Risk Non-Muscle Invasive Bladder Cancer

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

  • Nadofaragene Firadenovec — DRUG
    Vector-based gene therapy for NMIBC treatment to potentiate durable therapeutic responses by interferon (IFN) alfa-2b (IFN-α2b) amplification.

Study Details

A phase 3b, Randomized, Controlled Trial of Nadofaragene Firadenovec vs. Observation in Participants with Intermediate Risk Non-Muscle Invasive Bladder Cancer (IR NMIBC)

Key Dates

Start date
Oct 1, 2024
Status verified
May 2026
Primary completion
Jun 30, 2028
Completion
Jun 30, 2031

Study Design

Enrollment
454 participants (estimated)
Allocation
RANDOMIZED
Intervention model
PARALLEL
Primary purpose
TREATMENT

Arms

  • Experimental: Arm 1 Nadofaragene Firadenovec
    Participants in the nadofaragene firadenovec arm will receive quarterly instillations with nadofaragene firadenovec for 24 months. For these subjects, the disease evaluation visits will occur within 2 weeks prior to the investigation medicinal products instillation visits.
  • No Intervention: Arm 2 - Observation
    Subjects will be followed based on the surveillance schedule of the AUA/SUO guideline (quarterly) over the 24 months treatment period. .

Primary Outcome Measure

Recurrence Free survival [ Time Frame: 24 months ]

Central Contacts

Locations (49)

FacilityCityStateZIPSite coordinators
University of South Alabama (USA) Health System - USACMMobileAlabama36606-
Urology Associates of MobileMobileAlabama56608-
Mayo Clinic ArizonaPhoenixArizona85054-
Center for NeurosciencesTucsonArizona85718-
Arkansas Urology, North Little RockLittle RockArkansas72211-
Michael G Oefelein, MD Clinical TrialsBakersfieldCalifornia93301-
Urology Associates of Central CaliforniaFresnoCalifornia93720-
American Institute of ResearchLos AngelesCalifornia90017-
Urology Center of Southern CaliforniaMurrietaCalifornia92563-
University of California, IrvineOrangeCalifornia92868-
Providence Saint John's Cancer InstituteSanta MonicaCalifornia90404-
Advent HealthDenverColorado80210-
Medstar Georgetown University HospitalWashington D.C.District of Columbia20007-
Mayo ClinicJacksonvilleFlorida32224-
Advanced Urology institute - PinellasLargoFlorida33771-
Sarasota Memorial Healthcare SystemSarasotaFlorida34239-
Emory UniversityAtlantaGeorgia30322-
NextStage Clinical ResearchLisleIllinois60532-
Blessing Health SystemQuincyIllinois62301-
First Urology Research (Jeffersonville)JeffersonvilleIndiana47130-
Urology Center of Iowa ResearchCliveIowa50325-
Wichita Urology GroupWichitaKansas67226-
University of Kentucky (UK) - Markey Cancer CenterLexingtonKentucky40536-
Anne Arundel Urology, PAAnnapolisMaryland21401-
Mayo Clinic - Rochester MinnesotaRochesterMinnesota55905-
Mercy Clinic Oncology and Hematology - David C. Pratt Cancer CenterCreve CoeurMissouri63141-
Specialty Clinical Research of St. LouisSt LouisMissouri63141-
Adult and Pediatric Urology P.C.OmahaNebraska68114-
Atlantic HealthMorristownNew Jersey07960-
Albany Medical CollegeAlbanyNew York10461-
Great Lakes Physician PC d/b/a Western New York Urology AssociatesCheektowagaNew York14225-
AccuMed Research AssociatesGarden CityNew York11530-
Northwell Health -The Arthur Smith Institute for UrologyLake SuccessNew York11042-
Integrated Medical Professionals, PLLCNew YorkNew York10016-
Veterans Affairs New York Harbor Healthcare System - Manhattan VA Medical CenterNew YorkNew York10010-
Premier Medical Group of the Hudson ValleyPoughkeepsieNew York12603-
James J. Peters VA Medical CenterThe BronxNew York10468-
University of CincinnatiCincinnatiOhio45267-
Oregon Health and Science University (Portland)PortlandOregon97239-
MidLantic UrologyBala-CynwydPennsylvania19004-
Keystone Urology SpecialistsLancasterPennsylvania17601-
University of Pennsylvania - Perelman Center for Advanced Medicine - Penn UrologyPhiladelphiaPennsylvania19104-
University of Pittsburgh Medical Center - Shadyside Medical BuildingPittsburghPennsylvania15232-
Carolina Urologic Research CenterMyrtle BeachSouth Carolina29572-
Urology AustinAustinTexas78759-
Urology Clinics of North Texas PLLC (Dallas)DallasTexas75231-
Houston Methodist Hospital (Houston)HoustonTexas77030-
Houston Metro Urology - Memorial CityHoustonTexas77027-
Urology of VirginiaVirginia BeachVirginia23462-

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