Prospective Clinical Assessment Study in Children With Hypochondroplasia
Part of paid clinical trials in Oakland, California.
- Sponsor
- QED Therapeutics, a BridgeBio company
- Study ID
- NCT06410976
- Status
- Recruiting
Conditions
- Hypochondroplasia
Eligibility Criteria
- Sex
- ALL
- Age
- 30 Months - 16 Years
- Healthy Volunteers
- Not accepted
Study Details
This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).
Key Dates
- Start date
- Jun 5, 2024
- Status verified
- Oct 2025
- Primary completion
- Oct 31, 2026
- Completion
- Oct 31, 2026
Study Design
- Enrollment
- 150 participants (estimated)
Primary Outcome Measure
Annualized height velocity [ Time Frame: up to 3 years ]
Central Contacts
- QED Therapeutics, Inc1-877-280-5655
Locations (8)
| Facility | City | State | ZIP | Site coordinators |
|---|---|---|---|---|
| UCSF Benioff Children's Hospital | Oakland | California | 94609 | - |
| Childrens Hospital Colorado | Aurora | Colorado | 80045 | - |
| Children's National Hospital | Washington D.C. | District of Columbia | 20010 | - |
| Johns Hopkins School of Medicine | Baltimore | Maryland | 21287 | - |
| University of Missouri | Columbia | Missouri | 65201 | - |
| Cincinnati Children's Hospital Medical Center | Cincinnati | Ohio | 45229 | - |
| Vanderbilt University Medical Center | Nashville | Tennessee | 37232 | - |
| University of Wisconsin Madison - Waisman Center Bone Dysplasia Clinic | Madison | Wisconsin | 53705 | - |
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