Prospective Clinical Assessment Study in Children With Hypochondroplasia

Part of paid clinical trials in Oakland, California.

Sponsor
QED Therapeutics, a BridgeBio company
Study ID
NCT06410976
Status
Recruiting

Conditions

  • Hypochondroplasia

Eligibility Criteria

Sex
ALL
Age
30 Months - 16 Years
Healthy Volunteers
Not accepted

Study Details

This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).

Key Dates

Start date
Jun 5, 2024
Status verified
Oct 2025
Primary completion
Oct 31, 2026
Completion
Oct 31, 2026

Study Design

Enrollment
150 participants (estimated)

Primary Outcome Measure

Annualized height velocity [ Time Frame: up to 3 years ]

Central Contacts

Locations (8)

FacilityCityStateZIPSite coordinators
UCSF Benioff Children's HospitalOaklandCalifornia94609-
Childrens Hospital ColoradoAuroraColorado80045-
Children's National HospitalWashington D.C.District of Columbia20010-
Johns Hopkins School of MedicineBaltimoreMaryland21287-
University of MissouriColumbiaMissouri65201-
Cincinnati Children's Hospital Medical CenterCincinnatiOhio45229-
Vanderbilt University Medical CenterNashvilleTennessee37232-
University of Wisconsin Madison - Waisman Center Bone Dysplasia ClinicMadisonWisconsin53705-

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