A Multicenter Multinational Observational Study of Children With Hypochondroplasia

Part of paid clinical trials in Phoenix, Arizona.

Sponsor
BioMarin Pharmaceutical
Study ID
NCT06212947
Status
Recruiting
Apply to this trial

Conditions

  • Hypochondroplasia

Eligibility Criteria

Sex
ALL
Age
N/A - 15 Years
Healthy Volunteers
Not accepted

Study Details

This study will assess growth over time and the clinical course of HCH in children by collecting growth measurements and other variables of interest.

Key Dates

Start date
Nov 27, 2023
Status verified
Apr 2025
Primary completion
Dec 31, 2043
Completion
Dec 31, 2043

Study Design

Enrollment
400 participants (estimated)

Arms

  • Arm: Children with Hypochondroplasia
    Children with Hypochondroplasia

Primary Outcome Measure

Change in annualized growth velocity (AGV) [ Time Frame: Every 6 months through end of study, up to 15 years ]

Central Contacts

Locations (16)

FacilityCityStateZIPSite coordinators
Phoenix Children's HospitalPhoenixArizona85016-
Cedars-Sinai Medical CenterLos AngelesCalifornia90048-
UCSF Benioff Children's HospitalOaklandCalifornia94609-
Nemours Alfred I. Dupont Hospital for ChildrenWilmingtonDelaware19803-
Children's National Health SystemWashington D.C.District of Columbia20010-
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoIllinois60611-
The Johns Hopkins University School of MedicineBaltimoreMaryland21218-
Boston Children's HospitalBostonMassachusetts02115-
University of Minnesota Masonic Children's HospitalMinneapolisMinnesota55454-
University of MissouriColumbiaMissouri65212-
Washington University School of Medicine in St. LouisSt LouisMissouri63110-
Mount Sinai Kravis Children's HospitalNew YorkNew York10029-
Akron Children's HospitalAkronOhio44307-
Nationwide Children's HospitalColumbusOhio43205-
Cook Children's EndocrinologyFort WorthTexas76104-
Medical College of Wisconsin, Children's HospitalMilwaukeeWisconsin53226-

Find similar trials in Phoenix, AZ

By research site
Phoenix Children's Hospital· Phoenix, AZCedars-Sinai Medical Center· Los Angeles, CAUCSF Benioff Children's Hospital· Oakland, CANemours Alfred I. Dupont Hospital for Children· Wilmington, DEChildren's National Health System· Washington D.C., DCAnn & Robert H. Lurie Children's Hospital of Chicago· Chicago, IL

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