Effect of Theophylline in Pseudohypoparathyroidism

Part of paid clinical trials in Boston, Massachusetts.

Sponsor
Massachusetts General Hospital
Study ID
NCT03718403
Phase
PHASE4
Status
Recruiting

Conditions

  • PHP IB
  • PHP Ia
  • Php1C

Eligibility Criteria

Sex
ALL
Age
5 Years - 21 Years
Healthy Volunteers
Not accepted

Interventions

  • Theophylline — DRUG
    Theophylline will be given to maintain a peak level between 10-15 mcg/mL

Study Details

The study evaluates the effect of theophylline in 100 subjects with Pseudohypoparathyroidism.

Key Dates

Start date
Nov 11, 2019
Status verified
Jul 2022
Primary completion
Apr 10, 2030
Completion
Apr 10, 2032

Study Design

Enrollment
100 participants (estimated)
Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
OTHER

Arms

  • Experimental: Single arm open labeled intervention study
    Subjects with PHP will be given theophylline to decrease the end organ resistance by increasing levels of cAMP, a second messenger. Theophylline will be dosed twice a day for a period of 52 weeks.

Primary Outcome Measure

Effect of Theophylline on Bone Age in PHP [ Time Frame: 52 weeks ]

Central Contacts

Locations (1)

FacilityCityStateZIPSite coordinators
Massachusetts General HospitalBostonMassachusetts02114
Amita Sharma
617-726-2908

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