International Trial of Selumetinib in Combination With Dexamethasone for the Treatment of Acute Lymphoblastic Leukaemia
- Sponsor
- University of Birmingham
- Study ID
- NCT03705507
- Phase
- PHASE1/PHASE2
- Status
- Terminated
Conditions
- Acute Lymphoblastic Leukemia
- Acute Lymphoblastic Leukemia Recurrent
- Acute Lymphoblastic Leukemia, Adult
- Acute Lymphoblastic Leukemia, Pediatric
- Acute Lymphoblastic Leukemia, in Relapse
Eligibility Criteria
- Sex
- ALL
- Age
- N/A - N/A
- Healthy Volunteers
- Not accepted
Interventions
- Selumetinib — DRUGSelumetinib is a small molecule inhibitor of the MEK protein
- Dexamethasone — DRUGSteroid used for the treatment and management of a number of conditions including cancers and leukaemias.
Study Details
This trial is to investigate the combination of selumetinib and dexamethasone in the treatment of acute lymphoblastic leukaemia (ALL) in both adults and children. Phase I is to find the most suitable dose of selumetinib to safely give with dexamethasone. Phase II will use this dose to find out how well the combination works.
Key Dates
- Start date
- May 18, 2018
- Status verified
- May 2023
- Primary completion
- May 3, 2023
- Completion
- May 3, 2023
Study Design
- Enrollment
- 12 participants (actual)
- Allocation
- NON_RANDOMIZED
- Intervention model
- PARALLEL
- Primary purpose
- TREATMENT
Arms
- Experimental: Selumetinib + Dexamethasone - Group A (18 years and above)Patients will receive the adult cohort specified dose of selumetinib by mouth, as a single dose on cycle 1 day 1, then twice daily continuously from cycle 1 day 4 onwards. Combined with pulsed doses of dexamethasone at 6mg/m2/day on days 2-4 and 8-11 then at 4mg/m2/day on days 15-18 and 22-25 divided into two doses (as per local practice) by mouth during cycle 1, then on days 1-4 at 4mg/m2/day at the start of cycle 2, then on days 1-5 at 6mg/m2/day during subsequent cycles.
- Experimental: Selumetinib + Dexamethasone - Group P (under 18 years)Patients will receive the paediatric cohort specified dose of selumetinib by mouth, as a single dose on cycle 1 day 1, then twice daily continuously from cycle 1 day 4 onwards. Combined with pulsed doses of dexamethasone at 6mg/m2/day on days 2-4 and 8-11 then at 4mg/m2/day on days 15-18 and 22-25 divided into two doses (as per local practice) by mouth during cycle 1, then on days 1-4 at 4mg/m2/day at the start of cycle 2, then on days 1-5 at 6mg/m2/day during subsequent cycles.
Primary Outcome Measure
Phase I: The occurrence/non-occurrence of dose limiting toxicities (DLTs) in the trial defined assessment period [ Time Frame: During cycle 1 (each cycle is 28 days) ]
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