To Evaluate the Long-term Safety and Tolerability of Acoramidis in Participants With Newly Diagnosed ATTR-CM (ACT-EARLY OLE)
- Sponsor
- Eidos Therapeutics, a BridgeBio company
- Study ID
- NCT07116473
- Phase
- PHASE3
- Status
- Not Yet Recruiting
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Conditions
- Amyloid Cardiomyopathy
- Amyloid Cardiomyopathy, Transthyretin-Related
- Amyloidogenic Transthyretin (ATTR) Amyloidosis
- Amyloidosis
- Amyloidosis in Transthyretin (TTR)
- Amyloidosis, Familial
- Amyloidosis, Hereditary, Transthyretin-Related
- Cardiomyopathies
- Heart Disease
- Polyneuropathies
Eligibility Criteria
- Sex
- ALL
- Age
- 18 Years - N/A
- Healthy Volunteers
- Not accepted
Interventions
- Acoramidis (AG10) — DRUGTTR stabilizer administered orally twice daily (BID)
Study Details
The AG10-504 study is an open-label extension study of acoramidis in participants with newly diagnosed transthyretin amyloid cardiomyopathy (ATTR-CM) or both ATTR-CM and transthyretin amyloid polyneuropathy (ATTR-PN).
Key Dates
- Start date
- Nov 30, 2025
- Status verified
- Aug 2025
- Primary completion
- Nov 30, 2037
- Completion
- Dec 31, 2037
Study Design
- Enrollment
- 250 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: AcoramidisParticipants will receive acoramidis 712 mg orally BID (which is equivalent to 800 mg acoramidis HCl BID)
Primary Outcome Measure
To evaluate the long-term safety and tolerability of acoramidis in participants with newly diagnosed ATTR-CM [ Time Frame: The duration of study participation for the participants will be up to 5 years. ]
Central Contacts
- Medical Information1-415-887-1471
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