SARC046: A Phase II Trial of Nab-Sirolimus in Patients With Progressing or Symptomatic Epithelioid Hemangioendothelioma

Part of paid clinical trials in Stanford, California.

Sponsor
Sarcoma Alliance for Research through Collaboration
Study ID
NCT07104331
Phase
PHASE2
Status
Recruiting

Conditions

  • Epithelioid Hemangioendothelioma (EHE)

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

  • nab-Sirolimus — DRUG
    nab-Sirolimus 100 mg/m2 will be administered as an intravenous infusion over 30 minutes on Days 1 and 8 of each 21-day cycle.

Study Details

This is a non-randomized, open label, single arm Phase II trial with a two-stage design with histologically-confirmed metastatic and/or recurrent epithelioid hemangioendothelioma requiring systemic treatment. nab-Sirolimus 100 mg/m2 will be administered as an intravenous infusion over 30 minutes on Days 1 and 8 of each 21-day cycle. The primary objective is to determine ORR by RECIST v1.1 of nab-sirolimus in patients with EHE who require systemic treatment.

Key Dates

Start date
Feb 24, 2026
Status verified
May 2026
Primary completion
Aug 30, 2029
Completion
Aug 30, 2029

Study Design

Enrollment
41 participants (estimated)
Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT

Arms

  • Experimental: non-randomized, open label, single arm

Primary Outcome Measure

Tumor response rate [ Time Frame: Approximately 24 months ]

Locations (6)

FacilityCityStateZIPSite coordinators
Stanford UniversityStanfordCalifornia94305
Maria Ahern
650-725-6413
University of ColoradoAuroraColorado80203-
Brigham and Women's HospitalBostonMassachusetts02115-
Dana-Farber Cancer InstituteBostonMassachusetts02215
Dana-Farber Cancer Institute
877-338-7425
Michael Wagner, MD (PRINCIPAL_INVESTIGATOR)
Washington University St. LouisSt LouisMissouri63130
Cheryl Callahan
314-286-2584
Sloan Kettering Institute for Cancer ResearchNew YorkNew York10065
Jennifer Wu
646-888-6787

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