DMD Voice: Qualitative Interviews With Patients and Caregivers

Part of paid clinical trials in Yardley, Pennsylvania.

Sponsor
Red Nucleus Enterprise Solutions, LLC
Study ID
NCT06925269
Status
Recruiting
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Conditions

  • Duchenne Muscular Dystrophy (DMD)

Eligibility Criteria

Sex
MALE
Age
10 Years - N/A
Healthy Volunteers
Not accepted

Study Details

The purpose of this study is to understand DMD functional losses or abilities and their association with independence and quality of life from the perspective of individuals with DMD and/or and their caregivers. This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.

Key Dates

Start date
Mar 31, 2025
Status verified
Apr 2025
Primary completion
Dec 31, 2025
Completion
Dec 31, 2026

Study Design

Enrollment
68 participants (estimated)

Arms

  • Arm: Subsample A - Caregivers
    Caregivers of individuals with DMD treated with givinostat for at least 2 years
  • Arm: Subsample A - Patients
    Patients with DMD treated with givinostat for at least 2 years
  • Arm: Subsample B - Caregivers
    Caregivers of individuals with DMD never treated with givinostat

Primary Outcome Measure

Qualitative Interview [ Time Frame: 60 minutes ]

Central Contacts

Locations (1)

FacilityCityStateZIPSite coordinators
Red NucleusYardleyPennsylvania19067
Mary Hubbard
[email protected]
904-541-9326
Mindy Leffler (PRINCIPAL_INVESTIGATOR)

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By research site
Red Nucleus· Yardley, PA

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