Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Part of paid clinical trials in Los Angeles, California.
- Sponsor
- Friedreich's Ataxia Research Alliance
- Study ID
- NCT06016946
- Status
- Recruiting
Conditions
- Friedreich Ataxia
Eligibility Criteria
- Sex
- ALL
- Age
- N/A - N/A
- Healthy Volunteers
- Accepted
Study Details
This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.
Key Dates
- Start date
- Jun 28, 2023
- Status verified
- Jun 2025
- Primary completion
- Jan 28, 2048
- Completion
- Jan 28, 2048
Study Design
- Enrollment
- 3,000 participants (estimated)
Primary Outcome Measure
Change in modified Friedreich Ataxia Rating Scale (mFARS) Score [ Time Frame: Baseline, Year 1-25 ]
Central Contacts
- Cait Monette16513291892
- Jennifer Farmer14848796160
Locations (9)
| Facility | City | State | ZIP | Site coordinators |
|---|---|---|---|---|
| UCLA Ataxia Center | Los Angeles | California | 90095 | Susan Perlman, MD (PRINCIPAL_INVESTIGATOR) |
| University of Colorado | Denver | Colorado | 80045 | Trevor Hawkins, MD (PRINCIPAL_INVESTIGATOR) |
| University of Florida - Neurology | Gainesville | Florida | 32610 | general clinic line 1-352-294-5757 SH Subramony, MD (PRINCIPAL_INVESTIGATOR) |
| USF Ataxia Research Center | Tampa | Florida | 33612 | Theresa Zesiewicz, MD (PRINCIPAL_INVESTIGATOR) |
| Emory University Hospital - Neurology | Atlanta | Georgia | 30329 | UNIFAI Study 404-727-1509 George Wilmot, MD (PRINCIPAL_INVESTIGATOR) |
| University of Iowa, Stead Family Children's Hospital | Iowa City | Iowa | 52242 | general clinic line, 1-319-356-2436 Katherine Mathews, MD (PRINCIPAL_INVESTIGATOR) |
| Ohio State University - Neurology | Columbus | Ohio | 43221 | Chad Hoyle, MD (PRINCIPAL_INVESTIGATOR) |
| Children's Hospital of Philadelphia | Philadelphia | Pennsylvania | 19104 | David Lynch, MD PhD (PRINCIPAL_INVESTIGATOR) |
| St. Jude Children's Research Hospital | Memphis | Tennessee | 38105 | Richard Finkel, MD (PRINCIPAL_INVESTIGATOR) |
Find similar trials in Los Angeles, CA
Related Studies
- An Open-Label Study of CTI-1601 in Subjects With Friedreich's AtaxiaPHASE2 · Recruiting · Larimar Therapeutics, Inc. · Los Angeles, California
- A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own DoctorsRecruiting · Biogen · Los Angeles, California
- Clinical Course Of Disease In Participants With FA-CMRecruiting · Lexeo Therapeutics · La Jolla, California
- A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's AtaxiaPHASE3 · Recruiting · Biogen · Los Angeles, California