Safety and Tolerability of Ziftomenib Combinations in Patients With Relapsed/Refractory Acute Myeloid Leukemia

Part of paid clinical trials in Gilbert, Arizona.

Sponsor
Kura Oncology, Inc.
Study ID
NCT06001788
Phase
PHASE1
Status
Recruiting

Conditions

  • AML
  • AML With Mutated NPM1
  • Acute Leukemia
  • Acute Myeloid Leukemia
  • Hematologic Malignancy
  • KMT2Ar
  • Leukemia
  • Leukemia, Myeloid
  • Leukemia, Myeloid, Acute
  • MLL Rearrangement
  • NPM1 Mutation
  • Neoplasms by Histologic Type

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

  • Ziftomenib — DRUG
    Oral administration
  • Fludarabine — DRUG
    Intravenous infusion
  • Idarubicin — DRUG
    Intravenous infusion
  • Cytarabine — DRUG
    Intravenous Infusion
  • Gilteritinib — DRUG
    Oral administration
  • Granulocyte colony-stimulating factor — BIOLOGICAL
    Subcutaneous injection

Study Details

The safety, tolerability, and antileukemic response of ziftomenib in combination with standard of care treatments for patients with relapsed/refractory acute myeloid leukemia will be examined with the following agents: FLAG-IDA, low-dose cytarabine, and gilteritinib.

Key Dates

Start date
Feb 22, 2024
Status verified
Apr 2026
Primary completion
Aug 31, 2026
Completion
Aug 31, 2027

Study Design

Enrollment
171 participants (estimated)
Allocation
NON_RANDOMIZED
Intervention model
PARALLEL
Primary purpose
TREATMENT

Arms

  • Experimental: Phase 1a
    Oral ziftomenib; sequential cohorts of escalating dose levels of ziftomenib to identify the safety and tolerability of the combination regimens. Participants will be enrolled in 1 of 5 dose escalation cohorts: A-1: Participants with a NPM1 mutation: ziftomenib plus FLAG-IDA A-2: Participants with a NPM1 mutation: ziftomenib plus low-dose cytarabine (LDAC) A-3: Participants with a NPM1 mutation: ziftomenib plus gilteritinib B-1: Participants with a KMT2A rearrangement: ziftomenib plus FLAG-IDA B-2: Participants with a KMT2A rearrangement: ziftomenib plus low-dose cytarabine (LDAC)
  • Experimental: Phase 1b
    Oral ziftomenib; Following the determination of the maximum tolerated dose in Phase 1a, participants will be enrolled in 1 of 5 dose validation/expansion cohorts: A-1: Participants with a NPM1 mutation: ziftomenib plus FLAG-IDA A-2: Participants with a NPM1 mutation: ziftomenib plus low-dose cytarabine (LDAC) A-3: Participants with a NPM1 mutation: ziftomenib plus gilteritinib B-1: Participants with a KMT2A rearrangement: ziftomenib plus FLAG-IDA B-2: Participants with a KMT2A rearrangement: ziftomenib plus low-dose cytarabine (LDAC)

Primary Outcome Measure

Rate of dose limiting toxicities (DLTs) per dose level [ Time Frame: During the first 28 days of ziftomenib in combination with SOC treatment (1 cycle) ]

Central Contacts

Locations (38)

FacilityCityStateZIPSite coordinators
Banner MD Anderson Cancer CenterGilbertArizona85234
480-256-6444
UCLA Health - Bowyer Oncology CenterLos AngelesCalifornia90095
Bruck Habtemariam
310-794-0242
USC Norris Comprehensive Cancer CenterLos AngelesCalifornia90089
Christine Duran
323-865-0371
UC Irvine Health Chao Family Comprehensive Cancer CenterOrangeCalifornia92868
Research Line
877-827-8839
University of California San FranciscoSan FranciscoCalifornia94115-
Colorado Blood Cancer InstituteDenverColorado80218
New Patient Contact
720-754-4835
Smilow Cancer Hospital at Yale New HavenNew HavenConnecticut06511
Farah Fasihuddin
203-737-3472
Emory Healthcare - The Emory ClinicAtlantaGeorgia30322
Gigi Stoneback
Georgia Cancer Center at Augusta UniversityAugustaGeorgia30912
Amanda Spires
Robert H. Lurie Comprehensive Cancer Center of Northwestern UniversityChicagoIllinois60611
312-695-9367
Loyola University Medical CenterMaywoodIllinois60153
Esteban Orozco Espiricueta
708-327-3221
Simmons Cancer InstituteSpringfieldIllinois62702-
University of Iowa Hospitals & ClinicsIowa CityIowa52242
Grerk Sutamtewagul
319-353-8383
The University of Kansas Cancer CenterKansas CityKansas66160
KUCC Navigation Team
913-588-3671
Beth Israel Deaconess Medical CenterBostonMassachusetts02215-
Henry Ford Cancer InstituteDetroitMichigan48202
Kristyn Dailey
Karmanos Cancer InstituteDetroitMichigan48201-
Washington University School of MedicineSt LouisMissouri63110-
University of Nebraska Medical CenterOmahaNebraska68198-
John Theurer Cancer Center at Hackensack University Medical CenterHackensackNew Jersey07601
Oncology Clinical Reference Referral Office
551-996-1777
Roswell Park Comprehensive Cancer CenterBuffaloNew York14263
877-275-7724
Northwell Health, LLC PRIMELake SuccessNew York11042-
Memorial Sloan Kettering Cancer CenterNew YorkNew York10021
646-888-4167
Weill Cornell Medical College-NY Presbyterian HospitalNew YorkNew York10065
Tania Curcio
212-746-2571
Wilmot Cancer Institute, University of RochesterRochesterNew York14642
Clinical Trials Referral Office
855-776-0015
Stony Brook Cancer CenterStony BrookNew York11794
Zita Makselyte
Atrium Health Levine Cancer CenterCharlotteNorth Carolina60201
Chari Granger
UH Seidman Cancer CenterClevelandOhio44106
Leslie Ortega
216-844-8129
OU Health Stephenson Cancer CenterOklahoma CityOklahoma73104
Cynthia J Lowery
Lehigh Valley Topper Cancer InstituteAllentownPennsylvania18103-
Prisma HealthGreenvilleSouth Carolina29615
Lisa Johnson
864-455-3735
Fiona Davidson
864-455-3737
Vanderbilt University Medical CenterNashvilleTennessee37232
Recruitment and Eligibility Office
800-811-8480
Texas Oncology - Baylor Charles A. Sammons Cancer CenterDallasTexas75246
Christine Terraciano
MD Anderson Cancer CenterHoustonTexas77030
University of VermontBurlingtonVermont05401
Stephanie Stahl
802-656-2021
University of Virginia Comprehensive Cancer CenterCharlottesvilleVirginia22903
Avani Hopkins
434-243-8108
University of WashingtonSeattleWashington98109-
Froedtert & Medical College ClinicsMilwaukeeWisconsin53226-

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