Pegcetacoplan Long Term Safety and Efficacy Extension Study

Part of paid clinical trials in Los Angeles, California.

Sponsor
Apellis Pharmaceuticals, Inc.
Study ID
NCT03531255
Phase
PHASE3
Status
Completed

Conditions

  • PNH

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

Study Details

This is an Open-label, Non-Randomized, Multi-Center Extension Study. Eligible subjects will have previously completed a pegcetacoplan study.

Key Dates

Start date
Aug 27, 2018
Status verified
Mar 2026
Primary completion
Sep 4, 2025
Completion
May 19, 2026

Study Design

Enrollment
137 participants (actual)
Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT

Arms

  • Experimental: 1,080 mg pegcetacoplan administered subcutaneously
    1,080mg pegcetacoplan administered subcutaneously twice weekly or every three days.

Primary Outcome Measure

Incidence and severity of treatment-emergent adverse events [ Time Frame: Baseline to 2 Years ]

Locations (9)

FacilityCityStateZIPSite coordinators
University of Southern CaliforniaLos AngelesCalifornia90033-
Denver Health Medical CenterDenverColorado80204-
Cancer Specialists of North FloridaJacksonvilleFlorida32257-
Lakes ResearchMiamiFlorida33014-
Northwestern UniversityChicagoIllinois60611-
Investigative Clinical Research of IndianaIndianapolisIndiana46260-
Duke University Medical CenterDurhamNorth Carolina27710-
Cleveland ClinicClevelandOhio44195-
Baptist Cancer CenterMemphisTennessee38120-

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