Development of Clinical Database of Individuals With Smith-Magenis Syndrome and Sleep Disturbances

Part of paid clinical trials in Washington D.C., District of Columbia.

Sponsor
Vanda Pharmaceuticals
Study ID
NCT03154697
Status
Recruiting

Conditions

  • Sleep Disturbances in Smith-Magenis Syndrome

Eligibility Criteria

Sex
ALL
Age
3 Years - 65 Years
Healthy Volunteers
Not accepted

Interventions

  • Data collection of sleep disturbances in individuals with SMS — OTHER
    Data related to Smith-Magenis syndrome and sleep disturbances are collected through a web or phone survey

Study Details

This database will be used to better understand the sleep problems of people with SMS. This clinical database will be a part of a larger Smith-Magenis Patient Registry used to create an awareness campaign around SMS and the sleep disturbances that are characteristic of the disorder.

Key Dates

Start date
Jan 31, 2016
Status verified
Oct 2018
Primary completion
Dec 31, 2030
Completion
Dec 31, 2030

Study Design

Enrollment
1,000 participants (estimated)

Primary Outcome Measure

Number of individuals with Smith- Magenis syndrome [ Time Frame: 5 years ]

Central Contacts

Locations (1)

FacilityCityStateZIPSite coordinators
Vanda PharmaceuticalsWashington D.C.District of Columbia20037
Vanda Pharmaceuticals
202-734-3400

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