XEN1101 Clinical Trials (2026): 8 Studies for Focal Epilepsy & Focal Onset Seizures

Hipa.ai Research · Source: ClinicalTrials.gov / AACT

Synced daily from ClinicalTrials.gov via AACT. Last sync: .

8 XEN1101 clinical trials are catalogued on Hipa.ai from the AACT mirror of ClinicalTrials.gov, spanning 5 indications (including Focal Epilepsy & Focal Onset Seizures) and 2,323 total planned enrollment. 4 Phase 3 XEN1101 trials and 3 Phase 2 are listed. 3 XEN1101 clinical trials are actively recruiting at 68 U.S. sites across 27 states. Most recent activity: NCT05718817 (Jun 2033).

Where to Participate: All XEN1101 Trial Sites in the U.S. (68 sites across 27 states)

Every actively recruiting XEN1101trial site, sorted by state then city. Each row links to the trial detail page (eligibility, contacts, full study record). Sites no longer enrolling at the location level are excluded. ClinicalTrials.gov / AACT does not provide street-level addresses; the map link uses the facility's geocoded coordinates where available.

StateFacilityCityTrialMap
ALUniversity of Alabama - Strada Patient Care Center, NeurologyMobile36604NCT05667142Map
AZXenosciencePhoenix85004NCT05667142Map
AZUniversity of Arizona - Health Science CenterTucson85724NCT05667142Map
ARClinical Trials, Inc.Little Rock72205NCT05716100Map
ARUniversity of Arkansas for Medical SciencesLittle Rock72205NCT05667142Map
CARancho Research InstituteDowney90242NCT05716100Map
CABrain Science Research InstituteLos Angeles90025NCT05667142Map
CAUniversity of California Los Angeles (UCLA)Los Angeles90095NCT05716100Map
CAUniversity of California Irvine HealthOrange92868NCT05716100Map
CAUniversity of California, Irvine - Health Neurology ServicesOrange92868NCT05667142Map
COUniversity of Colorado Anschutz Medical CampusAurora80045NCT05667142Map
FLPanhandle Research and Medical ClinicGulf Breeze32651NCT05716100Map
FLMayo Clinic FloridaJacksonville32224NCT05667142Map
FLMayo Clinic FloridaJacksonville32224NCT05716100Map
FLSerenity Research Center, LLCMiami33176NCT05667142Map
FLPanhandle Research and Medical ClinicPensacola32503NCT05667142Map
FLMedsol Clinical Research Center Harbor Professional CentrePort Charlotte33952NCT05667142Map
FLUniversity of South FloridaTampa33606NCT05667142Map
FLEncore Medical Research of Weston, LLCWeston33331NCT05667142Map
GAChildren's Healthcare of AtlantaAtlanta30342NCT05667142Map
GAEmory Brain Health CenterAtlanta30329NCT05667142Map
HIHawaii Pacific Neuroscience, Comprehensive Epilepsy CenterHonolulu96817NCT05667142Map
IDConsultants in Epilepsy and Neurology, PLLCBoise83702NCT05667142Map
IDConsultants in Epilepsy and Neurology, PLLCBoise83702NCT05716100Map
ILSouthern Illinois University School of MedicineSpringfield62794NCT05667142Map
ILSouthern Illinois University School of MedicineSpringfield62794NCT05716100Map
KSUniversity of Kansas Medical CenterKansas City66160NCT05667142Map
KYBluegrass Epilepsy Research, LLCLexington40504NCT05667142Map
KYUniversity of Kentucky Albert B. Chandler Hospital (UK Healthcare)Lexington40536NCT05667142Map
MDMedStar Franklin Square Medical CenterBaltimore21237NCT05667142Map
MDUniversity of Maryland Medical CenterBaltimore21201NCT05667142Map
MDMid-Atlantic Epilepsy and Sleep CenterBethesda20817NCT05667142Map
MDMid-Atlantic Epilepsy and Sleep CenterBethesda20817NCT05716100Map
MDMedstar Georgetown University HospitalClinton20735NCT05667142Map
MABrigham and Women's HospitalChestnut Hill02467NCT05667142Map
MAUMass Memorial Medical CenterWorcester01655NCT05667142Map
MIUniversity of Michigan HospitalsAnn Arbor48109NCT05667142Map
MI9D University Health CenterDetroit48201NCT05716100Map
MIWayne State UniversityDetroit48201NCT05667142Map
MIMichigan State University Department of NeurologyEast Lansing48824NCT05667142Map
MISpectrum HealthGrand Rapids49503NCT05667142Map
MOSaint Louis University Medical SchoolSt Louis14624NCT05667142Map
NJNortheast Regional Epilepsy GroupHackensack07601NCT05667142Map
NJNortheast Regional Epilepsy GroupHackensack07601NCT05716100Map
NYSUNY Upstate Medical UniversitySyracuse13201NCT05667142Map
NCAtrium HealthCharlotte28203NCT05667142Map
NCOnsite Clinical Solutions, LLCCharlotte28211NCT05667142Map
NCDuke University ClinicDurham27705NCT05716100Map
NCDuke University Clinical ResearchDurham27710NCT05667142Map
NCWake Forest Baptist HealthWinston-Salem27104NCT05667142Map
OHSumma Health Clinical Research CenterAkron44304NCT05667142Map
OHCleveland ClinicCleveland44195NCT05716100Map
OHCleveland Clinic FoundationCleveland44195NCT05667142Map
OHOhioHealthColumbus43214NCT05716100Map
OHOhioHealth Riverside Methodist HospitalColumbus43214NCT05667142Map
OHThe Ohio State UniversityColumbus43210NCT05667142Map
ORProvidence Neurological SpecialitiesPortland97225NCT05716100Map
PATemple University HospitalPhiladelphia19140NCT05667142Map
PAUniversity of PennsylvaniaPhiladelphia19104NCT05667142Map
PAUPMC Comprehensive Epilepsy CenterPittsburgh15213NCT05667142Map
TNVanderbilt University Medical CenterNashville37232NCT05716100Map
TXAustin Epilepsy Care CenterAustin78758NCT05716100Map
TXANESC ResearchEl Paso79912NCT05667142Map
TXUTHealth Science Center at HoustonHouston77030NCT05667142Map
TXUniversity of Texas Health Science Center at San AntonioSan Antonio78229NCT05667142Map
VASentara Neurology SpecialistsVirginia Beach23456NCT05667142Map
WAUniversity of Washington, Regional Epilepsy Center at Harborview Medical CenterSeattle98104NCT05667142Map
WIAdvocate Aurora Research institute, St. Luke's Medical CenterMilwaukee53215NCT05667142Map

XEN1101 clinical trials at a glance: phase × recruitment status

Phaserecruitingactive not recruitingenrolling by invitationcompletedTotal
P111
P2123
P32114

Recruiting XEN1101 clinical trials (3)

Studies currently enrolling participants. Click any NCT ID to view the trial detail page (eligibility, sites, contacts).

NCT IDTitlePhaseIndicationEnrollmentStarted
NCT05718817X-TOLE4An Open-label Study of XEN1101 in EpilepsyP3Focal Epilepsy880Apr 2023
NCT05667142X-ACKTA Study to Evaluate XEN1101 as Adjunctive Therapy in Primary Generalized Tonic-Clonic SeizuresP3Primary Generalized Tonic-Clonic Seizures160Feb 2023
NCT05716100X-TOLE3A Randomized Study of XEN1101 Versus Placebo in Focal-Onset Seizures (X-TOLE3)P3Focal Onset Seizures360May 2023

XEN1101 clinical trials by indication

Focal Onset Seizures (2)

NCTAcronymPhaseStatusTitle
NCT05716100X-TOLE3P3recruitingA Randomized Study of XEN1101 Versus Placebo in Focal-Onset Seizures (X-TOLE3)
NCT05614063X-TOLE2P3completedA Randomized Study of XEN1101 Versus Placebo in Focal-Onset Seizures

Focal Epilepsy (2)

NCTAcronymPhaseStatusTitle
NCT05718817X-TOLE4P3enrolling by invitationAn Open-label Study of XEN1101 in Epilepsy
NCT03796962X-TOLEP2active not recruitingA Study to Evaluate XEN1101 as Adjunctive Therapy in Focal Epilepsy

Major Depressive Disorder (2)

NCTAcronymPhaseStatusTitle
NCT04827901P2completedXEN1101 for Major Depressive Disorder
NCT05376150X-NOVAP2completedA Study to Evaluate the Safety, Tolerability and Efficacy of XEN1101 in Major Depressive Disorder

Primary Generalized Tonic-Clonic Seizures (1)

NCTAcronymPhaseStatusTitle
NCT05667142X-ACKTP3recruitingA Study to Evaluate XEN1101 as Adjunctive Therapy in Primary Generalized Tonic-Clonic Seizures

Healthy Volunteers (1)

NCTAcronymPhaseStatusTitle
NCT04952467P1completedSingle-dose Mass Balance Recovery and Metabolite Profile and Identification of 14C-XEN1101

XEN1101 pivotal trial highlights (Phase 2/3/4)

Phase-2/3/4 studies with named acronyms — the registration-grade trials most cited in label discussions and Wikipedia.

AcronymNCTPhaseStatusIndicationEnrollmentPubMed
X-TOLE4NCT05718817P3enrolling by invitationFocal Epilepsy880
X-ACKTNCT05667142P3recruitingPrimary Generalized Tonic-Clonic Seizures160
X-TOLE3NCT05716100P3recruitingFocal Onset Seizures360
X-TOLE2NCT05614063P3completedFocal Onset Seizures380
X-TOLENCT03796962P2active not recruitingFocal Epilepsy325PMID 37812429
X-NOVANCT05376150P2completedMajor Depressive Disorder168PMID 40423966

All XEN1101 trials (8)

Sorted by most recent activity (completion → start → posted date). Each row links to the trial detail page on Hipa.ai.

NCT IDAcronymTitlePhaseStatusEnrollmentSponsorStarted
NCT05718817X-TOLE4An Open-label Study of XEN1101 in EpilepsyP3enrolling by invitation880Xenon Pharmaceuticals Inc.Apr 2023
NCT03796962X-TOLEA Study to Evaluate XEN1101 as Adjunctive Therapy in Focal EpilepsyP2active not recruiting325Xenon Pharmaceuticals Inc.Jan 2019
NCT05667142X-ACKTA Study to Evaluate XEN1101 as Adjunctive Therapy in Primary Generalized Tonic-Clonic SeizuresP3recruiting160Xenon Pharmaceuticals Inc.Feb 2023
NCT05716100X-TOLE3A Randomized Study of XEN1101 Versus Placebo in Focal-Onset Seizures (X-TOLE3)P3recruiting360Xenon Pharmaceuticals Inc.May 2023
NCT05614063X-TOLE2A Randomized Study of XEN1101 Versus Placebo in Focal-Onset SeizuresP3completed380Xenon Pharmaceuticals Inc.Nov 2022
NCT04827901XEN1101 for Major Depressive DisorderP2completed44James MurroughOct 2021
NCT05376150X-NOVAA Study to Evaluate the Safety, Tolerability and Efficacy of XEN1101 in Major Depressive DisorderP2completed168Xenon Pharmaceuticals Inc.May 2022
NCT04952467Single-dose Mass Balance Recovery and Metabolite Profile and Identification of 14C-XEN1101P1completed6Xenon Pharmaceuticals Inc.Jul 2021

XEN1101 clinical trials: frequently asked questions

How many XEN1101 clinical trials are there?
8 XEN1101 clinical trials are catalogued on Hipa.ai, sourced from the AACT mirror of ClinicalTrials.gov. 3 are actively recruiting participants. 4 are marked completed.
Are XEN1101 clinical trials recruiting in 2026?
Yes — 3 XEN1101 trials are actively recruiting in 2026, with 68 U.S. sites across 27 states. See the recruiting trials and the per-state site list further down this page.
What conditions is XEN1101 being studied for?
XEN1101 is being studied for Focal Epilepsy, Focal Onset Seizures, Major Depressive Disorder, Healthy Volunteers, Primary Generalized Tonic-Clonic Seizures and 1 more. The trials are grouped by indication on this page.
What phase is XEN1101 in?
XEN1101 clinical trials span 4 Phase 3, 3 Phase 2, 1 Phase 1. The phase × status matrix at the top of this page breaks down counts by phase and recruitment status.
Who sponsors XEN1101 clinical trials?
The lead sponsor across the most XEN1101 trials is Xenon Pharmaceuticals Inc., with 1 additional lead sponsor listed in the data. Each trial row links to the full study detail page including sponsor information.

Sources and methodology

Trial inventory derived from the AACT mirror of ClinicalTrials.gov. Trials are filtered to those naming XEN1101as an intervention. Phase, status, enrollment, sponsor, and dates are taken from the source `studies` table; primary indication is the first listed condition. Acronyms are extracted from each trial's brief title where present. PubMed links are populated for trials whose published primary outcomes have been indexed in our evidence cache.

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