Vosoritide Evidence: Trial Results and Peer-Reviewed Publications

Top peer-reviewed publications

Curated set of pivotal-trial result papers and recent publications in high-tier journals.

1. Rationale, design, and methods of a randomized, controlled, open-label clinical trial with open-label extension to investigate the safety of vosoritide in infants, and young children with achondroplasia at risk of requiring cervicomedullary decompression surgery.
   Savarirayan R, Irving M, Maixner W, et al. · Sci Prog · 2022
   PubMed: PMID 33761804 · NCT04554940 · Dwarfism
2. Vosoritide treatment for children with hypochondroplasia: a phase 2 trial.
   Dauber A, Zhang A, Kanakatti Shankar R, et al. · EClinicalMedicine · 2024
   PubMed: PMID 38813446 · NCT04219007 · Dwarfism

Publications by year

2022–2024: 2 publications.

Publications by indication

Publications by journal

• Sci Prog1 paper
• EClinicalMedicine1 paper

All Vosoritide publications (2)

Sources and methodology

• Publications: ctgov.study_references (PubMed PMIDs auto-attached by ClinicalTrials.gov to each trial), reference types RESULT, DERIVED, and BACKGROUND.
• Per-arm outcome values: ctgov.outcome_measurements joined to ctgov.design_outcomes where outcome_type = 'PRIMARY', restricted to phase PHASE3 and PHASE2/PHASE3.
• Publication metadata (title, journal, year, authors): PubMed E-utilities efetch.fcgi
• Data freshness: Tue, 26 May 2026 18:08:36 GMT.