Pegvaliase Clinical Trials (2026): 8 Studies for Phenylketonuria (PKU) & Phenylketonurias

Hipa.ai Research · Source: ClinicalTrials.gov / AACT

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8 Pegvaliase clinical trials are catalogued on Hipa.ai from the AACT mirror of ClinicalTrials.gov, spanning 4 indications (including Phenylketonuria (PKU) & Phenylketonurias) and 828 total planned enrollment. 2 Phase 3 Pegvaliase trials, 1 Phase 4 are listed. 4 Pegvaliase clinical trials are actively recruiting at 24 U.S. sites across 13 states. Most recent activity: NCT06305234 (Nov 2033).

Where to Participate: All Pegvaliase Trial Sites in the U.S. (24 sites across 13 states)

Every actively recruiting Pegvaliasetrial site, sorted by state then city. Each row links to the trial detail page (eligibility, contacts, full study record). Sites no longer enrolling at the location level are excluded. ClinicalTrials.gov / AACT does not provide street-level addresses; the map link uses the facility's geocoded coordinates where available.

StateFacilityCityTrialMap
COUniversity of ColoradoAurora80045NCT05813678Map
COUniversity of ColoradoAurora80045NCT06305234Map
GAEmory UniversityAtlanta30322NCT05813678Map
GAEmory UniversityAtlanta30322NCT06305234Map
ILNorthwestern UniversityChicago60611NCT05813678Map
ILNorthwestern UniversityChicago60611NCT06305234Map
INIndiana University School of MedicineIndianapolis46202NCT05813678Map
INRiley Children's Hospital/ Indiana University HealthIndianapolis46202NCT06305234Map
LATulane University Medical CenterNew Orleans70118NCT05813678Map
LATulane University School of MedicineNew Orleans70112NCT06305234Map
MABoston Children's HospitalBoston02215NCT05813678Map
MABoston Children's HospitalBoston02215NCT06305234Map
NCSyneos HealthWilmington28403NCT05579548Map
OROregon Health & Science UniversityPortland97239NCT06305234Map
OROregon Health and Science UniversityPortland97239NCT05813678Map
PAUniversity of Pittsburgh Medical CenterPittsburgh15224NCT05813678Map
PAUniversity of Pittsburgh Medical CenterPittsburgh15213NCT06305234Map
TNVanderbilt University Medical SchoolNashville37235NCT05813678Map
TNVanderbilt University Medical SchoolNashville37235NCT06305234Map
TXUniversity of Texas Southwestern Medical CenterDallas75390NCT05813678Map
TXUT Southwestern Medical CenterDallas75390NCT06305234Map
UTUniversity of UtahSalt Lake City84112NCT05813678Map
WIChildren's Wisconsin/Medical College of WisconsinMilwaukee53226NCT06305234Map
WIMedical College of WisconsinMilwaukee53226NCT05813678Map

Pegvaliase clinical trials at a glance: phase × recruitment status

Phaserecruitingactive not recruitingcompletednot yet recruitingTotal
P3112
P411
N/A325

Recruiting Pegvaliase clinical trials (4)

Studies currently enrolling participants. Click any NCT ID to view the trial detail page (eligibility, sites, contacts).

NCT IDTitlePhaseIndicationEnrollmentStarted
NCT06305234A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)Phenylketonuria (PKU)200Jan 2024
NCT05813678PALaceA Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)Phenylketonuria (PKU)450Jun 2022
NCT05579548PALominoA Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and BreastfeedingPhenylketonuria, Maternal50Nov 2022
NCT07477691IMPALAImmune Modulation During Palynziq® Treatment in Adults (IMPALA)P4Phenylketonuria12Mar 2026

Pegvaliase clinical trials by indication

Phenylketonuria (PKU) (4)

NCTAcronymPhaseStatusTitle
NCT06305234N/ArecruitingA Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)
NCT05813678PALaceN/ArecruitingA Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)
NCT05270837PEGASUSP3active not recruitingStudy to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria
NCT03694353P3completedSafety and Efficacy of Self Administered Injections of Pegvaliase (>40mg/Day Dose) in Adults With PKU

Phenylketonurias (2)

NCTAcronymPhaseStatusTitle
NCT05356377N/AcompletedPreliminary Study of Brain Effects of Palynziq-Related Changes in Phenylalanine in Individuals With PKU
NCT03792451N/AcompletedNutrition Status of Adults Treated With Pegvaliase

Phenylketonuria (1)

NCTAcronymPhaseStatusTitle
NCT07477691IMPALAP4not yet recruitingImmune Modulation During Palynziq® Treatment in Adults (IMPALA)

Phenylketonuria, Maternal (1)

NCTAcronymPhaseStatusTitle
NCT05579548PALominoN/ArecruitingA Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeeding

Pegvaliase pivotal trial highlights (Phase 2/3/4)

Phase-2/3/4 studies with named acronyms — the registration-grade trials most cited in label discussions and Wikipedia.

AcronymNCTPhaseStatusIndicationEnrollmentPubMed
IMPALANCT07477691P4not yet recruitingPhenylketonuria12
PEGASUSNCT05270837P3active not recruitingPhenylketonuria (PKU)55

All Pegvaliase trials (8)

Sorted by most recent activity (completion → start → posted date). Each row links to the trial detail page on Hipa.ai.

NCT IDAcronymTitlePhaseStatusEnrollmentSponsorStarted
NCT06305234A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)recruiting200BioMarin PharmaceuticalJan 2024
NCT05813678PALaceA Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)recruiting450BioMarin PharmaceuticalJun 2022
NCT05579548PALominoA Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeedingrecruiting50BioMarin PharmaceuticalNov 2022
NCT05270837PEGASUSStudy to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With PhenylketonuriaP3active not recruiting55BioMarin PharmaceuticalJun 2022
NCT07477691IMPALAImmune Modulation During Palynziq® Treatment in Adults (IMPALA)P4not yet recruiting12BioMarin PharmaceuticalMar 2026
NCT05356377Preliminary Study of Brain Effects of Palynziq-Related Changes in Phenylalanine in Individuals With PKUcompleted6University of Missouri-ColumbiaMay 2022
NCT03694353Safety and Efficacy of Self Administered Injections of Pegvaliase (>40mg/Day Dose) in Adults With PKUP3completed37BioMarin PharmaceuticalSep 2018
NCT03792451Nutrition Status of Adults Treated With Pegvaliasecompleted18Boston Children's HospitalJan 2019

Pegvaliase clinical trials: frequently asked questions

How many Pegvaliase clinical trials are there?
8 Pegvaliase clinical trials are catalogued on Hipa.ai, sourced from the AACT mirror of ClinicalTrials.gov. 3 are actively recruiting participants. 3 are marked completed.
Are Pegvaliase clinical trials recruiting in 2026?
Yes — 3 Pegvaliase trials are actively recruiting in 2026, with 24 U.S. sites across 13 states. See the recruiting trials and the per-state site list further down this page.
What conditions is Pegvaliase being studied for?
Pegvaliase is being studied for Phenylketonuria (PKU), Phenylketonurias, Phenylketonuria, Phenylketonuria, Maternal. The trials are grouped by indication on this page.
What phase is Pegvaliase in?
Pegvaliase clinical trials span 1 Phase 4, 2 Phase 3. The phase × status matrix at the top of this page breaks down counts by phase and recruitment status.
Who sponsors Pegvaliase clinical trials?
The lead sponsor across the most Pegvaliase trials is BioMarin Pharmaceutical, with 2 additional lead sponsors listed in the data. Each trial row links to the full study detail page including sponsor information.

Sources and methodology

Trial inventory derived from the AACT mirror of ClinicalTrials.gov. Trials are filtered to those naming Pegvaliaseas an intervention. Phase, status, enrollment, sponsor, and dates are taken from the source `studies` table; primary indication is the first listed condition. Acronyms are extracted from each trial's brief title where present. PubMed links are populated for trials whose published primary outcomes have been indexed in our evidence cache.

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