Apply to trial NCT06904261

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RecruitingPhase 3Drug trial

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

An open-label study to evaluate the safety, pharmacokinetics (PK), pharmacodynamics (PD), and efficacy of migalastat treatment in pediatric subjects 2 to \< 12 years of age with Fabry disease and with amenable GLA variants.

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  2. We forward your profile to the study team

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  3. The team reaches out to schedule screening

    Usually within a few business days, via the contact you give.

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