Apply to trial NCT06609889

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RecruitingGenetic intervention

A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease

This study will test the safety and efficacy of multiple doses of ION283 administered as intrathecal (IT) injections by lumbar puncture (LP). All subjects will receive ION283. The dose level of 15 mg will be studied in all subjects.

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  3. The team reaches out to schedule screening

    Usually within a few business days, via the contact you give.

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