Apply to trial NCT05682144

A few quick questions so the study team can decide if you might be a fit.

RecruitingPhase 1Biological intervention

ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS I

A first-in-human study using ISP-001 in patients with Mucopolysaccharidosis Type I Hurler-Scheie and Scheie.

How this works

  1. Answer a few questions

    About 5 to 10 minutes. Skip-friendly where possible.

  2. We forward your profile to the study team

    They see only the answers needed to decide if you can be screened.

  3. The team reaches out to schedule screening

    Usually within a few business days, via the contact you give.

We save your progress under this email so you can come back later, and the study team uses it to reach you.

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